Real-world evidence (RWE) has been at the forefront of pharmaceutical innovations. It plays an important role in transforming drug development from a process ai

Randomized controlled trials (RCTs) have traditionally served as the gold standard for generating evidence about medical interventions. However, RCTs have inher

The volume and complexity of information about individual patients is greatly increasing with use of electronic records and personal devices. Potential effects

This User’s Guide is intended to support the design, implementation, analysis, interpretation, and quality evaluation of registries created to increase unders

This book provides a broad overview of rare disease drug development. It offers unique insights from various perspectives, including third-party capital provide